Spring School 2019

71 days

4 hours

6 mins


Wednesday, 03.04.2019


Shuttle pick up from hotel


Public Engagement: TBC
How to get something published: TBC
Presentation skills: Graciana Diez-Roux

12:00-13:00 Lunch (not provided by ESGCT)
13:00-15:15 Welcome address: Alberto Auricchio & Hildegard Büning
Opening keynote: Andrea Ballabio
Keynote: Adrian Thrasher
Keynote: Juan Bueren
15:15-15:45 Coffee Break

Session 1: Spotlight on delivery tools
Retro-/lentiviral vectors: Axel Schambach
What you should know about AAV? Hildegard Büning
Immune responses to vectors administered in vivo with a focus on the use of LV: Anne Galy
Non-viral gene delivery: Zoltan Ivics

Historical talk on Pozzuoli area
17:45-22:00 Guided tour of Pozzuoli
Dinner in Pozzuoli
Coach back to Naples

Thursday, 04.04.2019

08:00 Shuttle pick up from hotel
09:00-10:45   Session 2: Spotlight on stem cells/iPSC
Generation of neurons from iPS/ES cells: Vania Broccoli
Haematopoietic stem cells - smart tools in gene therapy: Giuliana Ferrari

Keynote: Guangping Gao
10:45-11:15 Coffee break
11:15-13:00  Session 3: Gene & cell therapy for eye diseases
The retina as target for gene therapy: Alberto Auricchio
Clinical trials of gene therapy for inherited blindness: Robin Ali

Keynote: Cell and gene therapy by somatic stem cells: the paradigm of epithelial stem cells: Michele De Luca
13:00-14:00 Lunch in canteen
14:00-15:00  Session 4: Spotlight on skeletal and cardiac gene therapy strategies
Gene therapy of the cardiovascular system: Mauro Giacca
Gene therapy of muscle disease: Fulvio Mavilio
15:00-15:30 Coffee break
15:30-17:30 Genome editing in HSC: Pietro Genovese
Epigenomic modifications: Angelo Lombardo
Safer designer nucleases and their delivery: Anna Cereseto
Round table
Challenges & hurdles of genome editing: Ethics & regulatory affairs
Chair: Luigi Naldini
Participants: Anna Cereseto, Mauro Giacca
17:45-22:00 Sightseeing tour of Naples
Pizza in Naples

Friday, 05.04.2019

08:15 Shuttle pick up from hotel
09:30-11:00   Session 6: Gene therapy for liver
Gene therapy of haemophilia: past, present and future: Federico Mingozzi
MPS6/ Crigler Najar: Nicola Brunetti Pierri
Immune responses in gene therapy: Gloria Gonzalez Aseguinolaza
11:00-11:30 Coffee Break
11:30 - 12:30 Session 7: Gene & cell therapy for CNS
Gene therapy for Huntington's disease: Nathalie Cartier
New strategies for CNS gene therapy: Alessandro Fraldi
12:30-13:30 Lunch in canteen
13:30-15:00 Session 8: Immunotherapy & cancer
In vivo cancer immune therapy: Vincenzo Cerullo
Ex vivo cancer immune therapy: Chiara Bonini
Innovative genetic vaccines for infectious diseases and cancer: Antonella Folgori
15:00-15:30 Coffee break
15:30-17:30 Fondazione Telethon Multiple stakeholder collaborative model to develop Gene Therapies: Lucia Faccio, Telethon Foundation

Session 9: Gene and cell therapy of PID
From an idea to a product and beyond : Alessandro Aiuti

Closing keynote: Nearly 3 decades of gene and cell therapy - has gene therapy fulfilled its promise? Luigi Naldini

Closing: Hildegard Buning and Alberto Auricchio