XXVI Congress

59 days

6 hours

15 mins

This week in gene and cell therapy - 27 October 2017

Gene and cell therapy headlines 23 - 27 October

 

British healthcare cost agency NICE supports use of GSK's Strimvelis gene therapy for ASA-SCID

Oxford based company Genomics to work on treatments for MS with Biogen

New A -> T base editing enzyme extends potential correction of single base pair mutations    

CRISPR based REPAIR system edits RNA

uniQure to start clinical trials for haemophilia B in 2018

Shire to start clinical trials for haemophilia A after being granted orphan drug designation by FDA

bluebird bio publishes first data from Starbeam trial of gene therapy for adrenoleukodystrophy