Spring School 2019

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This week in gene and cell therapy - 22 June 2018

Gene and cell therapy headlines 15 - 22 June

bluebird bio presents data from Phase 1/2 trial of LentiGlobin gene therapy for thalassemia and prepares for registration in Europe

Chiesi granted FDA orphan drug designation for GPLSCD01 cell therapy for limbal stem cell deficiency (LSCD)

Cellectis joins movement towards off the shelf CAR-T cell therapies

Sarepta phase 1/2 trial of gene therapy for Duchenne muscular dystrophy shows promising early results