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This week in gene and cell therapy - 31 August 2018

Gene and cell therapy headlines 27 - 31 August


MeiraGTx' AAV-CNGA3 gene therapy for achromatopsia granted rare pediatric disease designation

CAR-T news: Novartis' Kymriah and Gilead's Yescarta approved by EMA, but UK's National Health Service rejects Yescarta as too expensive

bluebird bio and Gritstone Oncoloy announce partnership to develop cell therapy

Gene therapy effective and safe in rat model of epilepsy

Adverum's ADVM-022 gene therapy for macular degeneration granted investigational new drug status

Exon skipping gene therapy for Duchenne muscular dystrophy effective in dogs