Webcast: Gene therapy in ADA-SCID, new challenges and opportunities
New Horizons in the Management of ADA-SCID have published their new webcast on Gene therapy in ADA-SCID, new challenges and opportunities.
Their expert panel discuss topics ranging from the use of bone marrow transplantation for ADA-SCID to the new opportunities and challenges that gene therapy can bring for the management of this rare immune disorder, including issues like appropriate selection of patients for clinical trials, the importance of the latest long-term data and the regulatory process for this type of therapy option.
- Moderator: Prof. Fabio Candotti, Lausanne University Hospital, Lausanne, Switzerland
- Dr Claire Booth, UCL Great Ormond Street Institute of Child Health, London, UK
- Dr Manfred Hönig, University Medical Center, University of Ulm, Germany