

FDA approval of the Biologics License Application (BLA) for Waskyra, the first gene therapy for the treatment of Wiskott-Aldrich syndrome (WAS).
The ESGCT would like to congratulate Fondazione Telethon and HSR-TIGET on the milestone achievement of the FDA approval of WAS ex vivo gene therapy. Please see below their statement: We are honoured to share a moment of profound significance for us, for patients, families, and the scientific community. The U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for Waskyra , the first gene therapy for the treatment of Wiskott-Aldrich


2025-SEVILLE
The 32nd ESGCT Annual Congress took place in collaboration with SETGYC from 7-10 October 2025 at Fibes in Seville. Congress delegates can log in to their online registration portal to access the Congress abstract book, online programme, and Certificate of Attendance. Login here > Abstracts published by Human Gene Therapy will be available soon. Event Statistics (Click to enlarge) We are very grateful for the support of all our sponsors and partners.


Around the World: Oncology, Hematology, and Cancer-Focused Cell and Gene Therapy in India
Hosted as part of the AROUND THE WORLD SERIES in collaboration with the Coalition of International Gene Therapy Societies.


Claire Booth wins the Rosalind Franklin Society Award
Congratulations to Claire Booth, who received the Rosalind Franklin Society Special Award in Science given by Mary Ann Liebert, Inc. and the Rosalind Franklin Society.


Fondazione Telethon announces submission of MAA to EMA for Gene Therapy for the treatment of Wiskott-Aldrich Syndrome patients
Read the press release here for full details.


School Event at the ESGCT 2024 Annual Congress
More than 1000 school students attended an event organised by Fondazione Telethon at the ESGCT Congress in Rome. Watch the event video here.


ESGCT 2024 HEADLINE NUMBERS
2024 was a busy year for ESGCT! See a summary of our headline numbers here.


E-Seminar - ATMP Research in South America - 02 December
Join the latest e-Seminar organised by the Coalition of International Gene Therapy Societies


Australasian Gene and Cell Therapy Society 13th Biennial Meeting
Aerial UTS Function Centre, Sydney, from 30 October - 1 November 2024.


E-Seminar - Coalition of International Gene Therapy Societies- 26 September
When: Thursday 26 September 2024 Australian Eastern Standard Time (AEST): 10.00 PM Central European Summer Time (CEST): 2.00 PM Eastern...























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