NEWS BLOG

The Early Career Investigator Award recognises contributions made by ECRs.

This award is given each year to an individual or a team who has made a significant impact in the field of gene and cell therapy.

The Founders Award is given to an ESGCT senior scientist to celebrate key discoveries in gene and cell therapies.

The Early Career Investigator Award recognises contributions made by ECRs.

Gene and cell based approaches in neuromuscular disease Nantes, 14-16 January 2026 ESGCT is committed to the training and support of students and early career researchers, and the ESGCT Academy is a part of this remit. Each Academy is dedicated to a distinct topic and students undertaking a related PhD project are eligible to attend. The 2026 Academy focused on the development of gene and cell-based approaches in neuromuscular disease. The workshop provided the opportunity t

The ESGCT would like to congratulate Fondazione Telethon and HSR-TIGET on the milestone achievement of the FDA approval of WAS ex vivo gene therapy. Please see below their statement: We are honoured to share a moment of profound significance for us, for patients, families, and the scientific community. The U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for Waskyra , the first gene therapy for the treatment of Wiskott-Aldrich

The 32nd ESGCT Annual Congress took place in collaboration with SETGYC from 7-10 October 2025 at Fibes in Seville. Congress delegates can log in to their online registration portal to access the Congress abstract book, online programme, and Certificate of Attendance. Login here > Abstracts published by Human Gene Therapy will be available soon. Event Statistics (Click to enlarge) We are very grateful for the support of all our sponsors and partners.

Outstanding Achievement Award Juan Bueren, Ciemat, Madrid Professor Juan A. Bueren is a leading global expert in gene therapy and hematopoietic stem cell research, with pioneering contributions to treatments for rare diseases such as Fanconi Anemia (FA) and Leukocyte Adhesion Deficiency (LAD). He developed the first successful gene therapy for FA without prior conditioning—avoiding the toxicity of traditional transplantation—now under EMA and FDA review. He also led preclinic

Outstanding Achievement Award Chiara Bonini, Ospedale San Rafaelle, Milan Chiara Bonini, M.D., Professor of Hematology at the University Vita-Salute, San Raffaele, Head of the Experimental Hematology Unit of Ospedale San Raffaele. She was trained in Milano (Ospedale San Raffaele- OSR), New York (MSKCC) and Seattle (FHCRC). She has been a member of the Boards of ESGCT and ASGCT and chair of the EBMT CTIWP. She is currently member of the Board of ESH, member of the EHA Subcomm

Hosted as part of the AROUND THE WORLD SERIES in collaboration with the Coalition of International Gene Therapy Societies.

Congratulations to Claire Booth, who received the Rosalind Franklin Society Special Award in Science given by Mary Ann Liebert, Inc. and the Rosalind Franklin Society.

The 8th ESGCT Spring School took place in Potsdam, Germany from 8-11 April 2025. The Spring School was jointly organised with the German Society for Gene Therapy (DG-GT).

Read the press release here for full details.

More than 1000 school students attended an event organised by Fondazione Telethon at the ESGCT Congress in Rome. Watch the event video here.

2024 was a busy year for ESGCT! See a summary of our headline numbers here.

Join the latest e-Seminar organised by the Coalition of International Gene Therapy Societies

The 31st ESGCT Annual Congress took place in collaboration with SITGEC on 22-25 October 2024 at La Nuvola in Rome. The Human Gene Therapy abstract publication is available at https://www.liebertpub.com/doi/10.1089/hum.2024.63331.oab . Fondazione Telethon School Event Fondazione Telethon organised a special event to allow secondary school students to discover what the concrete impact of advanced therapies already is and where the medicine of the future is going. More than 100

This meeting will connect a broad network of researchers who share a common goal of using CRISPR-based genome engineering approaches to...

Aerial UTS Function Centre, Sydney, from 30 October - 1 November 2024.

When: Thursday 26 September 2024 Australian Eastern Standard Time (AEST): 10.00 PM Central European Summer Time (CEST): 2.00 PM Eastern...