NEWS BLOG

The ESGCT would like to congratulate Fondazione Telethon and HSR-TIGET on the milestone achievement of the FDA approval of WAS ex vivo gene therapy. Please see below their statement: We are honoured to share a moment of profound significance for us, for patients, families, and the scientific community.    The U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for  Waskyra , the  first gene therapy for the treatment of Wiskott-Aldrich

Start of employment 01.01.2026, temporary We are seeking an experienced postdoctoral researcher for developing and preclinical testing of innovative cell and gene therapy. Our laboratory is established at the Institute for Regenerative Medicine (IREM, www.irem.uzh.ch ) , a leading research institute of the University of Zurich (UZH) at the life-science research campus in Schlieren (ZH). We have a long-standing track record of gene therapy bench-to-bedside development for inhe

The 32nd ESGCT Annual Congress took place in collaboration with SETGYC from 7-10 October 2025 at Fibes in Seville. Congress delegates can log in to their online registration portal to access the Congress abstract book, online programme, and Certificate of Attendance. Login here > Abstracts published by Human Gene Therapy will be available soon. Event Statistics (Click to enlarge) We are very grateful for the support of all our sponsors and partners.

Outstanding Achievement Award Juan Bueren, Ciemat, Madrid Professor Juan A. Bueren is a leading global expert in gene therapy and hematopoietic stem cell research, with pioneering contributions to treatments for rare diseases such as Fanconi Anemia (FA) and Leukocyte Adhesion Deficiency (LAD). He developed the first successful gene therapy for FA without prior conditioning—avoiding the toxicity of traditional transplantation—now under EMA and FDA review. He also led preclinic

Outstanding Achievement Award Chiara Bonini, Ospedale San Rafaelle, Milan Chiara Bonini, M.D.,  Professor of Hematology at the University Vita-Salute, San Raffaele, Head of the Experimental Hematology Unit of Ospedale San Raffaele. She was trained in Milano (Ospedale San Raffaele- OSR), New York (MSKCC) and Seattle (FHCRC). She has been a member of the Boards of ESGCT and ASGCT and chair of the EBMT CTIWP. She is currently member of the Board of ESH, member of the EHA Subcomm

TIGEM, an internationally renowned research center dedicated to understanding genetic diseases and developing transformative therapies,...

Location : University Hospital Tübingen, Division of Translational Oncology Position Type : Full-time, 2 years with possible extension...

Hosted as part of the AROUND THE WORLD SERIES in collaboration with the Coalition of International Gene Therapy Societies.

Fondazione Telethon launches a new training initiative for early-career scientists at its flagship Institutes Fondazione Telethon is a...

The San Raffaele Telethon Institute for Gene Therapy (SR-TIGET - www.sr-tiget.it ) is seeking tenure-track GROUP LEADERS wishing to...

Congratulations to Claire Booth, who received the Rosalind Franklin Society Special Award in Science given by Mary Ann Liebert, Inc. and the Rosalind Franklin Society.

The 8th ESGCT Spring School took place in Potsdam, Germany from 8-11 April 2025. The Spring School was jointly organised with the German...

Read the press release here for full details.

More than 1000 school students attended an event organised by Fondazione Telethon at the ESGCT Congress in Rome. Watch the event video here.

Research technician position ( https://ingm.org/en/albanese-lab-eng/ ). The successful candidate will contribute to the establishment of...

A Lab Technician/Research Assistant position is immediately available in the Process Development Lab (PDL), led by Marina Radrizzani at...

2024 was a busy year for ESGCT! See a summary of our headline numbers here.

Join the latest e-Seminar organised by the Coalition of International Gene Therapy Societies

The 31st ESGCT Annual Congress took place in collaboration with SITGEC on 22-25 October 2024 at La Nuvola in Rome. The Human Gene Therapy abstract publication is available at https://www.liebertpub.com/doi/10.1089/hum.2024.63331.oab . Fondazione Telethon School Event Fondazione Telethon organised a special event to allow secondary school students to discover what the concrete impact of advanced therapies already is and where the medicine of the future is going. More than 100

This meeting will connect a broad network of researchers who share a common goal of using CRISPR-based genome engineering approaches to...