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FDA approval of the Biologics License Application (BLA) for Waskyra, the first gene therapy for the treatment of Wiskott-Aldrich syndrome (WAS).
The ESGCT would like to congratulate Fondazione Telethon and HSR-TIGET on the milestone achievement of the FDA approval of WAS ex vivo gene therapy. Please see below their statement: We are honoured to share a moment of profound significance for us, for patients, families, and the scientific community. The U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for Waskyra , the first gene therapy for the treatment of Wiskott-Aldrich
Gaëlle Jamar
Dec 10, 20251 min read


2025-SEVILLE
The 32nd ESGCT Annual Congress took place in collaboration with SETGYC from 7-10 October 2025 at Fibes in Seville. Congress delegates can log in to their online registration portal to access the Congress abstract book, online programme, and Certificate of Attendance. Login here > Abstracts published by Human Gene Therapy will be available soon. Event Statistics (Click to enlarge) We are very grateful for the support of all our sponsors and partners.
Emma Clare
Nov 7, 20251 min read


Around the World: Oncology, Hematology, and Cancer-Focused Cell and Gene Therapy in India
Hosted as part of the AROUND THE WORLD SERIES in collaboration with the Coalition of International Gene Therapy Societies.
Gaëlle Jamar
Jul 7, 20251 min read


Claire Booth wins the Rosalind Franklin Society Award
Congratulations to Claire Booth, who received the Rosalind Franklin Society Special Award in Science given by Mary Ann Liebert, Inc. and the Rosalind Franklin Society.
Emma Clare
May 6, 20251 min read


Fondazione Telethon announces submission of MAA to EMA for Gene Therapy for the treatment of Wiskott-Aldrich Syndrome patients
Read the press release here for full details.
Emma Clare
Feb 5, 20251 min read


School Event at the ESGCT 2024 Annual Congress
More than 1000 school students attended an event organised by Fondazione Telethon at the ESGCT Congress in Rome. Watch the event video here.
Emma Clare
Jan 15, 20251 min read


ESGCT 2024 HEADLINE NUMBERS
2024 was a busy year for ESGCT! See a summary of our headline numbers here.
Emma Clare
Jan 8, 20251 min read


E-Seminar - ATMP Research in South America - 02 December
Join the latest e-Seminar organised by the Coalition of International Gene Therapy Societies
Emma Clare
Nov 21, 20241 min read


Australasian Gene and Cell Therapy Society 13th Biennial Meeting
Aerial UTS Function Centre, Sydney, from 30 October - 1 November 2024.
Emma Clare
Oct 7, 20241 min read


E-Seminar - Coalition of International Gene Therapy Societies- 26 September
When: Thursday 26 September 2024 Australian Eastern Standard Time (AEST): 10.00 PM Central European Summer Time (CEST): 2.00 PM Eastern...
Gaëlle Jamar
Sep 17, 20241 min read


Call for Conference Grants: Apply Now for GenE-Humdi ITC Grants
Supporting the attendance and participation at the upcoming ESGCT Congress for students from ITC and NNC countries.
Emma Clare
Aug 9, 20241 min read


Gloria Gonzalez Aseguinolaza wins the Rosalind Franklin Society Award
Congratulations to Gloria Gonzalez Aseguinolaza, who received the Rosalind Franklin Society Special Award in Science given by Mary Ann Liebert, Inc. and the Rosalind Franklin Society.
Emma Clare
Jul 18, 20241 min read


e-SEMINAR WITH FEDERICA ESPOSITO AND IVANA TRAPANI
Hosted as part of the AROUND THE WORLD SERIES in collaboration with the Coalition of International Gene Therapy Societies.
Emma Clare
Jul 15, 20241 min read


Momentum in Cell and Gene Therapy Symposium, June 19 in Evry
Please attend our upcoming event, the Momentum in Cell and Gene Therapy Symposium which is co-organized by ART-TG (Inserm) and...
Gaëlle Jamar
Apr 23, 20241 min read


New plan announced to get more children access to cutting-edge, proven gene therapy treatments for rare diseases
Great Ormond Street Hospital (GOSH), supported by LifeArc and Great Ormond Street Hospital Children’s Charity (GOSH Charity), has...
Gaëlle Jamar
Apr 10, 20241 min read


VIVEbiotech announces significant growth in 2023
San Sebastián, Spain, December 14, 2023 - VIVEbiotech, S.L., a GMP contract development and manufacturing organization (CDMO) full...
Christina Slater
Dec 18, 20231 min read


FDA Investigating Serious Risk of T-cell Malignancy
FDA Investigating Serious Risk of T-cell Malignancy Following BCMA-Directed or CD19-Directed Autologous Chimeric Antigen Receptor (CAR) T...
Gaëlle Jamar
Nov 30, 20231 min read


Nobel Prize in Medicine 2023
The ESGCT would like to congratulate Katalin Karikó and Drew Weissman for their discoveries concerning nucleoside base modifications that...
Gaëlle Jamar
Oct 2, 20231 min read


VIVEbiotech participates in the European MAGIC project
The MAGIC consortium is committed to making a meaningful impact on the lives of individuals affected by muscular dystrophies.
Christina Slater
Jul 20, 20231 min read


Abstract submission deadline for the ETRS-SPCE annual meeting has been extended to July 16
Annual meeting of the European Tissue Repair Society (ETRS) and Portuguese Society of Stem Cells and Cell Therapies (SPCE), October 2023.
Christina Slater
Jul 12, 20231 min read
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