NEWS BLOG

The ESGCT would like to congratulate Fondazione Telethon and HSR-TIGET on the milestone achievement of the FDA approval of WAS ex vivo gene therapy. Please see below their statement: We are honoured to share a moment of profound significance for us, for patients, families, and the scientific community.    The U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for  Waskyra , the  first gene therapy for the treatment of Wiskott-Aldrich

The 32nd ESGCT Annual Congress took place in collaboration with SETGYC from 7-10 October 2025 at Fibes in Seville. Congress delegates can log in to their online registration portal to access the Congress abstract book, online programme, and Certificate of Attendance. Login here > Abstracts published by Human Gene Therapy will be available soon. Event Statistics (Click to enlarge) We are very grateful for the support of all our sponsors and partners.

Hosted as part of the AROUND THE WORLD SERIES in collaboration with the Coalition of International Gene Therapy Societies.

Congratulations to Claire Booth, who received the Rosalind Franklin Society Special Award in Science given by Mary Ann Liebert, Inc. and the Rosalind Franklin Society.